Rare Diseases and Orphan Products: Accelerating Research and Development
- ISBN-10
- 0309158060
- ISBN-13
- 9780309158060
- Category
- Medical
- Pages
- 442
- Language
- English
- Published
- 2011-04-03
- Publisher
- National Academies Press
- Authors
- Institute of Medicine, Board on Health Sciences Policy, Committee on Accelerating Rare Diseases Research and Orphan Product Development
Description
Rare diseases collectively affect millions of Americans of all ages, but developing drugs and medical devices to prevent, diagnose, and treat these conditions is challenging. The Institute of Medicine (IOM) recommends implementing an integrated national strategy to promote rare diseases research and product development.
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